Healthcare providers involved in diagnosing and treating rare diseases believe that increased physician education and collaboration with specialized facilities will have the greatest positive impact on treating these conditions over the next five years, according to results from a 2021 survey. Definitive Healthcare, a healthcare commercial intelligence company, conducted…
Increased Education Crucial to Improving Rare Disease Care, Survey Finds
An extract of the plant Lemna minor L., also called duckweed, suppresses the signs and symptoms of idiopathic pulmonary fibrosis (IPF) in disease-induced mice, a study suggests. More research to evaluate dosing and oral availability is recommended, study authors noted. “Pulmonary Protein Oxidation and Oxidative Stress…
One of my biggest fears is being a nuisance to others. As much as possible, I try not to rely on anyone and have learned to become stubbornly independent. This is why living with idiopathic pulmonary fibrosis (IPF), a debilitating and life-threatening lung disease, has been so hard on me:…
Lung Therapeutics’ LTI-03, an investigational inhaled therapy for idiopathic pulmonary fibrosis (IPF), was safe and well-tolerated in healthy volunteers, with no reports of serious adverse events (side effects) or discontinuations, according to a Phase 1a trial. “We are pleased that LTI-03 has passed this important safety milestone as…
This is not easy to talk about. I don’t even want to discuss it with my husband. I already feel awkward being intimate while wearing a nasal cannula and don’t want to add another unsexy health issue. My husband and I have always had a strong attraction to each other.
The word “identity,” which refers to a person’s “distinguishing character or personality,” according to Merriam-Webster, may sound simple to understand, but it’s actually often confused with other terms. Before you read any further, take a moment to think about your own identity. When you have a description in mind, please…
Coenzyme Q10 (CoQ10), an antioxidant found naturally in the body and some foods, may help airway basal stem cells survive and ease symptoms of idiopathic pulmonary fibrosis (IPF), a study in mice given both in a transplant suggests. Researchers observed that more airway basal stem cells, a type of…
The Translational Genomics Research Institute (TGen) will use a big-memory technology, called MemVerge Memory Machine Big Memory virtualization software, to accelerate research on the cellular mechanisms underlying idiopathic pulmonary fibrosis (IPF). “MemVerge Memory Machine has quickly resulted in research value for TGen,” Jonathan Jiang, chief operating officer of…
Trevi Therapeutics announced that CANAL, its proof-of-concept Phase 2 trial evaluating Haduvio (nalbuphine extended-release tablets) for the treatment of chronic cough in people with idiopathic pulmonary fibrosis (IPF) has finished enrolling. The trial (NCT04030026), which is taking place in the U.K., has enrolled about 40 IPF patients…
Patient registries are a hot topic of rare disease research and many organizations are taking advantage of this resource by signing up their patient communities and connecting with researchers. Eric Sid, MD, program officer for the Office of Rare Diseases Research (ORDR), said it is difficult to estimate how…
